Our purpose
We aim to make a significant impact on care and therapy for patients with neuromuscular disorders by understanding disease heterogeneity, leading to design and implementation of personalized interventions that are evidence-based. (Photo by Stichting Voor Sara)
Goals
- Enrich biobanks and registries
- Standardization of imaging biomarkers
- Develop muscle-on-a-chip technology
- Comparative preclinical evaluation of therapeutic approaches
- Identify molecular pathways underlying disease heterogeneity and drug targets
- Engage pediatric and adult patients in definition of most relevant, robust and sensitive outcome measures
- Model natural history to predict disease progression and use as base line in trials
- Design and execute platform trials
- Optimize 'zorgpaden' and allied health care
Research group leaders
See which research group leaders (RGLs) contribute to this research program.
read moreResearch group leaders
Our programs form inspiring environments in which research groups work together toward a common and clear goal, enabling our researchers to strenghten collaboration and cross thematic and disciplinary boundaries. Within and outside Radboudumc.
RGLs contributing to this research program
- Hans van Bokhoven
- Roland Brock
- Baziel van Engelen
- Peter-Bram 't Hoen
- Leo Joosten
- Dirk Lefeber
- Jorik Nonnekes
- Nicol Voermans
- Philip van der Wees
- Gert Jan van der Wilt
- Tom Scheenen
- Chris de Korte
In the near future, we plan to link specially designed research group pages instead of these profile pages.